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Disease ReportsFamilial amyloid neuropathies
MeSH D028227 - familial amyloid neuropathies
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
D020271:Nervous system heredodegenerative disorders
0 Companies
0 Drugs
Success rate
D017772:Amyloid neuropathies
0 Companies
0 Drugs
Success rate
D028226:Familial amyloidosis
$
Success rate
D028227: 
Familial amyloid neuropathies
$
Success rate
Events Timeline
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Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
Akcea TherapeuticsInotersen Tegsedi 2023-03-21 2018-10-05 $17.1 M Q1/19-Q1/20 
Alnylam PharmaceuticalsVutrisiran Amvuttra  2022-09-15 $749.284 M Q3/23-Q2/24 
Clinical Trials
Historical Success Rate
Phase 1
100%
1/1
Phase 2
75%
3/4
Phase 3
50%
3/6
Approved: 2Overall Success rate: 38%
All Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Company name
Phase 1
Phase 2
Phase 3
Phase 4
Drug Name
Akcea Therapeutics
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