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Familial amyloid neuropathies
MeSH D028227 - familial amyloid neuropathies
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Competitive Landscape
Events Timeline
Commercial
Clinical Trials
Competitive landscape
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D020271:
Nervous system heredodegenerative disorders
0 Companies
0 Drugs
Success rate
D017772:
Amyloid neuropathies
0 Companies
0 Drugs
Success rate
D028226:
Familial amyloidosis
1 Company
1 Drug
$
Success rate
D028227:
Familial amyloid neuropathies
2 Companies
2 Drugs
$
Success rate
Events Timeline
Commercial
Company Name
Drug Name
Trade Name
Patent Expires
Approval Date
Revenue
Period
Akcea Therapeutics
Inotersen
Tegsedi
2023-03-21
2018-10-05
$17.1 M
Q1/19-Q1/20
Clinical Trials
Historical Success Rate
Phase 1
100
%
1/1
Phase 2
75
%
3/4
Phase 3
50
%
3/6
Approved:
2
Overall Success rate:
38%
All Clinical Trials
Therapeutic Areas:
All
Classification:
All
Approval:
All
Status:
All
Phases:
All
Company name
Phase 1
Phase 2
Phase 3
Phase 4
Drug Name
Akcea Therapeutics
Inotersen
Alnylam Pharmaceuticals
Vutrisiran
,
Revusiran
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